Welcome to NARYA Genome Editing !
The future of gene therapy for microsatellite expansion disorders
Trinucleotide expansion disorders
Trinucleotide expansion disorders are dramatic neurodegenerative genetic diseases due to the expansion of a short DNA repeat. As of today, more than 30 such diseases have been identified, representing millions of patients worldwide, for whom no cure is available.
At NARYA GE, we use AI-optimized DNA endonucleases to shorten the expanded repeat tract under the pathological length. We aim at using these nucleases as gene therapy treament for these disorders. We are especially focused right now on Steinert disease and Huntington’s disease.
About NARYA Genome Editing
NARYA Genome Editing (NARYA GE) was founded by Dr Guy-Franck Richard, a molecular geneticist with more than 25 years of experience in genome editing. He has a PhD in molecular genetics, as well as an Habilitation à Diriger des Recherches.
He has been working at the Institut Pasteur for 25 years, as well as in Brandeis University (Waltham, USA) and Johns Hopkins University (Baltimore, USA).
Guy-Franck Richard uses highly specific AI-optimized DNA endonucleases to precisely edit and modify genomes with high efficacy and specificity. These nucleases are used to shorten trinucleotide repeats expanded in Steinert disease and Huntington disease to non-pathological lengths.
Guy-Franck Richard is also a consultant in genomics and gene therapy and gives advanced courses in eukaryotic genomics.
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